This Month In Muscular Dystrophy
Dr. Louise Rodino-Klapac Discusses Advances in Dysferlin Gene Therapy
- Autor: Vários
- Narrador: Vários
- Editora: Podcast
- Duração: 0:10:20
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Dr. Louise Rodino-Klapac Discusses Advances in Dysferlin Gene Therapy Guest: Louise Rodino-Klapac, PhD, principal investigator, Center for Gene Therapy, The Research Institute at Nationwide Children’s Hospital Access an abstract of this month’s featured research article: Homologous Recombination Mediates Functional Recovery of Dysferlin Deficiency following AAV5 Gene Transfer. PLoS One. 2012;7(6):e39233. Epub 2012 Jun 15.